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Guidance Documents/Guidance-Document/Innovative Designs for Clinical Trials of Cellular and Gene Therapy Products in Small Populations: Draft Guidance for Industry

Innovative Designs for Clinical Trials of Cellular and Gene Therapy Products in Small Populations: Draft Guidance for Industry

Detailed guidance document from FDA and regulatory agencies.

Document Details

Guidance Document

September 24, 2025

September 24, 2025

Center for Biologics Evaluation and Research

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